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Advancing industry-leading Dualase  genome editors as transformative medicines

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Dualase  uniquely overcomes the limitations and challenges of in vivo genome editing through its two-site mechanism, which enables seamless removal, repair and insertion of small or large sequences
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Dualase

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A differentiated genome editing platform delivering predictable and efficient edits with undetectable off-target effects and plug-and-play programmability for broad in vivo therapeutic applications

Pipeline

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Pipeline of in vivo therapeutics where small Dualase  genome editors have a differentiated mechanism of action coupled with single AAV or lipid nanoparticle / polymer encapsulated all-RNA delivery with initial focus on precise removal of expanded DNA repeats

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Programs in CNS, lung and liver indications where Dualase   editors accurately correct the underlying genetic driver of disease with the potential for durable benefits for patients with limited existing therapeutic options
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In the News

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